Lysosomes Catalytic dysfunction GM2 ganglioside depletion GM3 ganglioside accumulation Epileptic spasms Gross deletion Isozymes Substrate reduction therapy HEXA gene Warren Tay Hebephrenic schizophrenia Hypomyelination Infantile TSD = high HexA levels Founder effect N- acetylgalactosamine GLUT1 Dysphasia GM2- gangliosidosis HexB deficiency Chromosome 5q13.3 αR424 Autosomal- recessive White matter Gastrostomy tube HPβCD Flexible loop HexA α- subunit AAV vectors GM2 ganglioside accumulation Adult TSD = low HexA levels N- acetylneuraminic acid Hydrolysis Partial deletions Microglia Homodimeric PP6D5 polymer Ataxia Juvenile TSD = most severe Bernard Tay Miglustat GM3- gangliosidosis Infantile form Glycosphingolipid iPSC cells Decerebrate posturing Blood- brain barrier c.533 G > A Neuronal cells β- hexosaminidase A Proteolytic processing Neuroglia Chromosome 15q23 GM2 activator protein HEXB = chromosome 15 Autosomal- dominant Cherry- red spot 1 in 300 carriers Aspiration pneumonia Optic atrophy Grey matter Chromosome 15q13.3 Lysosomal storage metabolic disorder Warren Sachs Missense mutations Lysosomes Catalytic dysfunction GM2 ganglioside depletion GM3 ganglioside accumulation Epileptic spasms Gross deletion Isozymes Substrate reduction therapy HEXA gene Warren Tay Hebephrenic schizophrenia Hypomyelination Infantile TSD = high HexA levels Founder effect N- acetylgalactosamine GLUT1 Dysphasia GM2- gangliosidosis HexB deficiency Chromosome 5q13.3 αR424 Autosomal- recessive White matter Gastrostomy tube HPβCD Flexible loop HexA α- subunit AAV vectors GM2 ganglioside accumulation Adult TSD = low HexA levels N- acetylneuraminic acid Hydrolysis Partial deletions Microglia Homodimeric PP6D5 polymer Ataxia Juvenile TSD = most severe Bernard Tay Miglustat GM3- gangliosidosis Infantile form Glycosphingolipid iPSC cells Decerebrate posturing Blood- brain barrier c.533 G > A Neuronal cells β- hexosaminidase A Proteolytic processing Neuroglia Chromosome 15q23 GM2 activator protein HEXB = chromosome 15 Autosomal- dominant Cherry- red spot 1 in 300 carriers Aspiration pneumonia Optic atrophy Grey matter Chromosome 15q13.3 Lysosomal storage metabolic disorder Warren Sachs Missense mutations
(Print) Use this randomly generated list as your call list when playing the game. There is no need to say the BINGO column name. Place some kind of mark (like an X, a checkmark, a dot, tally mark, etc) on each cell as you announce it, to keep track. You can also cut out each item, place them in a bag and pull words from the bag.
Lysosomes
Catalytic dysfunction
GM2 ganglioside depletion
GM3 ganglioside accumulation
Epileptic spasms
Gross deletion
Isozymes
Substrate reduction therapy
HEXA gene
Warren Tay
Hebephrenic schizophrenia
Hypomyelination
Infantile TSD = high HexA levels
Founder effect
N-acetylgalactosamine
GLUT1
Dysphasia
GM2-gangliosidosis
HexB deficiency
Chromosome 5q13.3
αR424
Autosomal-recessive
White matter
Gastrostomy tube
HPβCD
Flexible loop
HexA α-subunit
AAV vectors
GM2 ganglioside accumulation
Adult TSD = low HexA levels
N-acetylneuraminic acid
Hydrolysis
Partial deletions
Microglia
Homodimeric
PP6D5 polymer
Ataxia
Juvenile TSD = most severe
Bernard Tay
Miglustat
GM3-gangliosidosis
Infantile form
Glycosphingolipid
iPSC cells
Decerebrate posturing
Blood-brain barrier
c.533 G > A
Neuronal cells
β-hexosaminidase A
Proteolytic processing
Neuroglia
Chromosome 15q23
GM2 activator protein
HEXB = chromosome 15
Autosomal-dominant
Cherry-red spot
1 in 300 carriers
Aspiration pneumonia
Optic atrophy
Grey matter
Chromosome 15q13.3
Lysosomal storage metabolic disorder
Warren Sachs
Missense mutations